Publications
2 shownCRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis
In a small group of patients with hereditary ATTR amyloidosis with polyneuropathy, administration of NTLA-2001 was associated with only mild adverse events and led to decreases ...
Frequent Co-Authors
Researcher Info
- h-index
- 2
- Publications
- 2
- Citations
- 2,224
- Institution
- Regeneron (United States)
External Links
Identifiers
- ORCID
- 0000-0001-8214-489X
Impact Metrics
h-index
2
h-index: Number of publications with at least h citations each.